With funds raised from the AHC Foundation, we will support AAV gene therapy and other research related to the project. We believe a path has been identified to a viable permanent treatment: gene therapy. The gene therapy we propose will involve inserting a functional copy of the ATP1A3 gene into a virus (an adeno-associated virus or AAV) that has been stripped of its harmful payload and its ability to reproduce. The virus will then be injected into the cerebrospinal fluid and will carry the functional gene to the cells in the brain that are failing. By delivering additional functional copies of the gene, we should be able to rescue those cells, and treat the disease permanently.
SEAN GERBER
With funds raised from the AHC Foundation, we will support AAV gene therapy and other research related to the project. We believe a path has been identified to a viable permanent treatment: gene therapy. The gene therapy we propose will involve inserting a functional copy of the ATP1A3 gene into a virus (an adeno-associated virus or AAV) that has been stripped of its harmful payload and its ability to reproduce. The virus will then be injected into the cerebrospinal fluid and will carry the functional gene to the cells in the brain that are failing. By delivering additional functional copies of the gene, we should be able to rescue those cells, and treat the disease permanently.
Learn more about the project here.
| Supporters | |||
| Name | Date | Amount | Comments |
| Kait Campos | 04/14/2021 | $104.37 | You're an inspiration, Sean!! We love you. | Aliya Thaler | 01/01/2021 | $206.28 | Linda Shropshire | 12/29/2020 | $52.34 | Nicolas Djiounas | 12/28/2020 | $7,576.77 | Ken and Yoko Clark | 12/15/2020 | $257.78 | Dennis Najjar | 12/10/2020 | $15,152.53 | This donation is on behalf of AccountingDepartment.com, LLC | Anonymous Friend | 12/09/2020 | $103.30 | Patti and Lenny Drapeau | 12/08/2020 | $104.37 | Go Sean Go! | Sandy & John Gerber | 12/08/2020 | $206.28 | Love, Santa | Kasey & Steve Damato | 12/08/2020 | $104.37 | We love you Sean! | Josh Robbins | 12/08/2020 | $260.46 | Señor Sangria | 12/08/2020 | $309.27 | Bill with your energy and passion we are confident you will find a cure. | Tara Nau | 12/08/2020 | $51.80 | William Christman | 12/08/2020 | $520.60 | Vanita Medlang | 12/07/2020 | $26.33 | Jill/Michael Thaler | 12/07/2020 | $103.30 | Bill...Keep up your courageous efforts. You're doing a great job!! | Tricia DiPiazza | 12/07/2020 | $416.55 | From Jim & Joe Berkery, Berkery Noyes | Josh Bopp | 12/07/2020 | $515.24 | Joseph Appelbaum | 12/07/2020 | $185.68 | Stay strong and never give up! | Charlie Letson | 12/07/2020 | $52.34 | Robert Milman | 12/07/2020 | $520.60 | Robert Milman | 12/07/2020 | $520.60 | Richard Villone | 12/07/2020 | $500.00 | Terri Johnson | 12/07/2020 | $51.52 | Anthony Ramirez | 12/05/2020 | $103.30 | Good luck to you Sean, stay strong! | Don Schiavone | 12/05/2020 | $520.60 | Josh Reid | 12/05/2020 | $1,040.89 | Keep up the good work!! | Laura Redmond | 12/05/2020 | $103.30 | Keep up the good work! | Barbara Bell | 12/04/2020 | $104.37 | Monica Vazquez Paredes | 12/04/2020 | $103.30 | Love Monica,Freddy, Zaida, and kids. Always in our prayers. | Anonymous Friend | 12/04/2020 | $103.30 | William Springer | 12/04/2020 | $104.37 | Anonymous Friend | 12/04/2020 | $103.30 | Anonymous Friend | 08/30/2020 | $51.80 | In loving memory of Lenore Burokoff | Anonymous Friend | 08/26/2020 | $51.80 | In loving memory of my lifetime friend Lenore Burokoff. | Anonymous Friend | 08/26/2020 | $51.80 | In loving memory of Lenore Burokoff. | Anonymous Friend | 08/17/2020 | $103.30 | Anonymous Friend | 08/15/2020 | $200.00 | In loving memory of Lenore Burokoff. | Anonymous Friend | 08/14/2020 | $51.80 | In memory of our very special Aunt Lenore. With lots of love, Marlene & Joseph | Anonymous Friend | 08/14/2020 | $103.30 | Anonymous Friend | 08/13/2020 | $103.30 | In loving memory of Lenore and continued caring for Sean. | Anthony S Gallicchio | 02/09/2020 | $20.00 | Dennis Najjar | 02/04/2020 | $10,000.00 | Djiounas Family Foundation | 01/16/2020 | $5,000.00 | Anonymous Friend | 01/02/2020 | $50.00 | Southern Maine Senior Golfers' Association | 08/05/2019 | $250.00 | Love you Sean | Joelle Mackey | 05/17/2019 | $.00 | Susan Fandacone | 05/17/2019 | $.00 | Joelle Mackey | 05/17/2019 | $100.00 | Anonymous Friend | 04/26/2019 | $25.00 | Anonymous Friend | 04/26/2019 | $50.00 |
| Total | $46,401.51 | ||